Hemophilia Insights

Our research summaries provide insights into the latest scientific...

Latest Research

Our research summaries provide insights into the latest scientific developments. Check back in our next newsletter for updates.

Clinical Trials

This is a list of upcoming or ongoing clinical trials that are actively recruiting and have been listed or updated in the last two weeks:
A Study to Investigate the Safety and Effectiveness of a Coagulation Factor IX Gene Insertion Therapy (REGV131-LNP1265) in Pediatric, Adolescent and Adult Participants With Hemophilia B
Study Type
Phase II
Location
2 countries
Age Range
18+ Years
Enrollment
130
A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Efficacy of NXT007 in Persons With Severe or Moderate Hemophilia A
Study Type
Phase II
Location
6 countries
Age Range
2 - 59 Years
Enrollment
60
Recombinant Single-chain Factor VIII (rVIII-SingleChain) in Chinese Participants With Hemophilia A Previously Treated With FVIII Products
Study Type
Phase III
Location
China
Age Range
0 - 65 Years
Enrollment
60
To Evaluate the Clinical Study of GS1191-0445 Injection in the Treatment of Hemophilia A
Study Type
Phase III
Location
China
Age Range
18 - 65 Years
Enrollment
50

Community News

World Federation of HemophiliaWorld Federation of HemophiliaApr 25, 2025

Exciting news! Sanofi and Sobi, together with the WFH and WFH USA have announced the second renewal of a five-year contract to provide support to the WFH Humanitarian Aid Program in the form of treatment product donations and financial assistance allowing the WFH to continue to deliver aid to people with inherited bleeding disorders across the globe. Learn more: https://bit.ly/4cRk167

World Federation of Hemophilia Post
The Haemophilia Society UKThe Haemophilia Society UKApr 28, 2025

There were tears (of joy), there were smiles, there were blisters and a LOT of confetti! London Marathon 2025 completed!! 🥇✅

We couldn't possibly be prouder of our 12 incredible runners. Xan, Mark, Steve, Alfie, Isla, Maggie, Jo, Lauren, Amy, Mareska, Kate and Luke. Congratulations to each and every one of you - you are AMAZING!

If you're feeling inspired and would like to run next year's race - the ballot is now open and closes this Friday 2 May. You can enter here https://www.londonmarathonevents.co.uk/london-marathon/enter-ballot

We have a really limited number of charity places so we ask everyone who wants to represent THS to first apply through the ballot. We'll then give as many charity places to those who are unsuccessful as we can.

You can still donate to the 2025 team here https://www.justgiving.com/campaign/thsmarathon25

The Haemophilia Society UK Post
Hemophilia of GeorgiaHemophilia of GeorgiaApr 28, 2025

#ThankYou – A huge shout out to all of our generous sponsors for this year's Trot to Clot Walk/Run! With your continued partnership and support we raised over $92,000 for youth and family programming, including Camp Wannaklot!

Sponsors:

Ameris Bank

Mauldin & Jenkins

Genentech

Kedrion

North Atlanta Primary Care

Sanofi

Takeda

Bayer

CSL Behring

Hema Biologics

Novo Nordisk

Octapharma

Merrill Lynch

Gallagher

New Image Roofing

Hemophilia of Georgia Post

Upcoming Events

APR
30
Advocacy call for Medicaid cuts Online Hemophilia Federation of America • Washington D.C., DC
MAY
19
Webinar on iron deficiency anemia Online Hemophilia Federation of America • Washington D.C., DC