Hemophilia Insights

This week's must-know community updates, latest research & events

March 26, 2025 • Estimated Reading Time: 1 minute

New Report: Introduction to Cell Therapy

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The report is available for free online on the AllMyHealth website.

www.allmyhealth.io/reports

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Latest Research

Hemophilia A is being explored as a candidate for hematopoietic stem cell therapies, particularly gene therapy, due to its unique characteristics related to factor VIII activity levels Shelton (2025).

These findings highlight the importance of early intervention and ongoing research into hemophilia treatments.

Clinical Trials

This is a list of upcoming or ongoing clinical trials that are actively recruiting and have been listed or updated in the last two weeks:

BeCoMe-9: a Clinical Study of BE-101 for the Treatment of Adults with Moderately Severe or Severe Hemophilia B

SAFE Study: Safety of APCC Following Emicizumab Prophylaxis

Recombinant Single-chain Factor VIII (rVIII-SingleChain) in Chinese Participants With Hemophilia A Previously Treated With FVIII Products

Haemophilia and Bone Loss - PHILEOS Study

View the full list of clinical trials →

Community News

Hemophilia Federation of AmericaMar 21, 2025

🎉 Bleeding Disorders Trivia Time! 🎉

We have some fun trivia to raise awareness for bleeding disorders, and we want YOU to get involved! 💡

Each week, we’ll pick 2 winners across all of our socials to win a t-shirt of your choice from our Limited Edition Bleeding Disorders Awareness Collection. These t-shirts are available ONLY until the end of the month, with proceeds benefiting our Helping Hands program, which helps those in the bleeding disorders community with financial support. Even better – proceeds will be generously matched by the Alliance Pharmacy! 🙌 https://hubs.li/Q03c3ZCq0

🎯 How to Enter:

Comment below with your answer to today’s question. We’ll pick two winners at random across all of our socials. Please do not click on any links in chat as we will message you if you win. Only US residents, please. 📩

👇 Here’s today’s trivia question: What nationality was Dr. Erik von Willebrand for which von Willebrand disease is named? He discovered the disease in a 5-year-old girl, of the same nationality, in 1924?

Hint: The answer can be found somewhere on our website!

Let's have some fun and raise awareness for bleeding disorders! 💙

Hemophilia of GeorgiaMar 25, 2025

#ThankYou - We are grateful to our generous sponsors, participants, and volunteers for your support of our Score Fore a Cure fundraising event! You helped make Score an incredible success and your contributions helped raise over $35,000 for bleeding disorder research. We couldn’t do it without you!

World Federation of HemophiliaMar 19, 2025

The WFH has been informed that Takeda has announced the global discontinuation of its #HemophiliaA treatments, HEMOFIL® M and RECOMBINATE. The WFH is aware that transitioning to other products can be challenging. Takeda informed the WFH that they are actively reaching out to healthcare professionals and WFH national member organizations to support the transition. Read more: https://bit.ly/4kE45HS